FDA Adds Orphan Disease Drugs To Expanded Access Navigator Tool

November 3, 2017 at 3:46 PM
FDA Commissioner Scott Gottlieb announced Thursday (Nov. 2) that FDA is expanding its Expanded Access Navigator, which aims to facilitate pre-approval access to drugs , to include drugs that treat orphan diseases. “Making sure there’s a close relationship with the efforts we take to expand pre-approval access to promising treatments, and the work of our orphan drugs program, is a key step toward maximizing opportunities for patients,” Gottlieb wrote in an FDA Voice blog. The move will help patients gain...


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