FDA Approves First CRISPR Gene Therapy, Affordability Questions Remain

By Jessica Karins, Maaisha Osman / December 8, 2023 at 12:27 PM

FDA approved for the first time a CRISPR-based genetic therapy, the sickle cell treatment exagamglogene autotemcel (exa-cel), a major step forward for the highly watched technology considered by many to have great potential for addressing genetic diseases.


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