Advocates Urge FDA To Set Up Rare Disease Center Of Excellence

By Beth Wang / December 5, 2019 at 11:07 AM
Rare disease advocates, gathered on Capitol Hill Wednesday (Dec. 4), made a plea for Congress and FDA to push policies aimed at spurring development of rare disease treatments. One of their requests: FDA should establish a rare disease center of excellence. The proposal for a rare disease COE has been raised before. And while FDA officials have said the idea isn’t off the table, they have also said there’s already enough integration among the agency centers that a COE is...

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